Natural history, outcome measures and trial readiness in LAMA2-related muscular dystrophy and SELENON-related myopathy in children and adults: protocol of the LAST STRONG study.

Author(s)Bouman K, Groothuis J T, Doorduin J, van Alfen N, Udink ten Cate F E, van den Heuvel F, Nijveldt R, van Tilburg W, Buckens S C, Dittrich A, Draaisma J M.
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